Xenpozyme is indicated as an enzyme replacement therapy for the treatment of non-Central Nervous System (CNS) manifestations of Acid Sphingomyelinase Deficiency (ASMD) in paediatric and adult patients with type A/B or type B.
MeSH: Acid sphingomyelinase deficiency (ASMD) type A/B or type B
Group: Other alimentary tract and metabolism products